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GOALS OF THERAPY
Prolong survival Delay progression Maintain function/quality of life Manage symptoms
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CLINICAL TRIALS: CONSIDER AT EVERY LINE
Strongly encourage enrollment in clinical trials, including studies of: CDK4 inhibitors (combinations) MDM2 inhibitors Immunotherapy combinations Novel targeted agents Cellular therapies Refer to clinicaltrials.gov
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FUTURE DIRECTIONS
Biomarker Development: CDK4 amplification, RB1 status, cell cycle signatures Rational Combinations: CDK4 inhibitor + MDM2 inhibitor; CDK4 inhibitor + immune therapy; CDK4 inhibitor + other targeted agents Overcoming Resistance: Identify resistance mechanisms and optimal sequencing/combination strategies Patient-Centered Care: Optimize QOL, symptom control, shared decision-making through all lines
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Diagnostic workup (at sarcoma center)
Suspected WDLPS/DDLPS: Expert pathology review with testing for MDM2 amplification MRI (extremity) or CT abdomen/pelvis (retroperitoneal) CT chest staging Core needle biopsy if needed Multidisciplinary tumor board review Discussion of surgery, radiation, systemic therapy, and clinical trials